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Eradicate dormant cancer cells: a programme to wake and kill or lock asleep disseminated cells

Many relapses come from cancer cells that hid dormant for years. Find drugs that either force them awake so chemotherapy kills them, or keep them asleep for life.

Disseminated tumour cells in bone marrow and other niches survive therapy in a quiescent state maintained by niche signals (TGF-beta 2, BMP, NR2F1, autophagy) and cause late relapse in breast, prostate and melanoma. Preclinical work shows both awakening strategies (sensitising to chemotherapy) and dormancy-enforcing strategies (NR2F1 agonists, 5-azacytidine plus retinoic acid, CDK4/6 inhibitors) can reduce metastasis. The proposal is a coordinated programme: standardised dormant-cell models, biomarkers of dormancy burden in patients (bone marrow and ctDNA), and adjuvant trials of dormancy-directed therapy in patients with detected disseminated cells.

Hypothesis
A dormancy-directed adjuvant regimen reduces late relapse (beyond three years) in high-risk hormone-receptor-positive breast cancer by a third compared with standard endocrine therapy.
Rationale
Late relapse is the dominant failure mode in several common cancers and no current therapy targets the dormant state; the biology is now tractable and measurable.
What would test it
Phase 2 randomised trial in patients with detectable disseminated tumour cells after standard adjuvant therapy, with disseminated cell clearance and distant recurrence as endpoints.
Maturity
preclinical evidence
Who has to act
research
Cost to try
Large (over $50M)
Years to first evidence
10
Bottlenecks it attacks

Connected

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