OnCo
trialsTrialPositive

FOENIX-CCA2

Futibatinib produced responses in over 40% of patients whose bile duct cancer carried an FGFR2 fusion.

ORR 42%, median PFS 9.0 months, median OS 21.7 months (NEJM 2023).

Setting
Previously treated FGFR2-rearranged intrahepatic cholangiocarcinoma: futibatinib single arm
Phase
Phase 2
Sponsor
Taiho
Registry
Headline result
ORR 42%; PFS 9.0 months; OS 21.7 months.
Reported
2022
Enrolled
103

Outcomes

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In plain words
What these results mean for people, not percentages
103 people took part
Objective response rateprimaryresponse endpoint
  • 42 out of 100 people had their tumour shrink with Futibatinib.
  • There was no comparison group, so this number cannot tell you how much of the effect is due to the treatment.
  • A response rate counts how many people had their tumours shrink by a set amount; shrinking is encouraging but does not by itself show that people live longer or feel better.
Progression-free survivalsurrogate endpoint
  • Median 9 months with Futibatinib.
  • A median is a midpoint: half the people did better than this and half did worse.
  • This is a surrogate endpoint: it measures the cancer being controlled or absent on scans and tests, which often, but not always, translates into living longer.
Overall survivalsurvival endpoint
  • Median 21.7 months with Futibatinib.
  • A median is a midpoint: half the people did better than this and half did worse.
  • Overall survival counts deaths from any cause, so it is the most direct measure of whether a treatment helps people live longer.
Be careful
  • These results apply to the people the trial enrolled: Previously treated FGFR2-rearranged intrahepatic cholangiocarcinoma: futibatinib single arm. People in a different situation may not see the same effect.
  • The trial selected people by a biomarker (FGFR2); the result should not be assumed for people whose cancer does not have it.

Numbers are from the trial as recorded here; see the source links in the table below. This is orientation, not medical advice: ask your team how closely the trial population matches you.

103 participants enrolled.

Objective response rateprimary
Futibatinib42 of 100
n = 103
Progression-free survival
Futibatinib
9 mo
Overall survival
Futibatinib
21.7 mo
EndpointArmnValueHR (95% CI)pSource
Objective response rateprimaryFutibatinib10342%
Progression-free survivalFutibatinib9 months
Overall survivalFutibatinib21.7 months

Connected

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