OnCo

MITF (Microphthalmia-associated transcription factor) is a protein that switches other genes on and off. The public catalogues list it as a drug target and a biomarker, and clinical evidence ties its variants to diagnosis, prognosis or drug response. Tied to Skin cancer, Breast cancer, Ovarian cancer and 2 more. This dossier gathers the 0 products (0 approved), 0 trials, 0 pathways and 0 resistance routes in the corpus that involve it, with external identifiers so it can be joined to UniProt, ChEMBL, Open Targets and the rest of biology.

Biology

Transcription factor that acts as a master regulator of melanocyte survival and differentiation as well as melanosome biogenesis. Binds to M-boxes (5'-TCATGTG-3') and symmetrical DNA sequences (E-boxes) (5'-CACGTG-3') found in the promoter of pigmentation genes, such as tyrosinase (TYR). Involved in the cellular response to amino acid availability by acting downstream of MTOR: in the presence of nutrients, MITF phosphorylation by MTOR promotes its inactivation. Upon starvation or lysosomal stress, inhibition of MTOR induces MITF dephosphorylation, resulting in transcription factor activity. Plays an important role in melanocyte development by regulating the expression of tyrosinase (TYR) and tyrosinase-related protein 1 (TYRP1). Plays a critical role in the differentiation of various cell types, such as neural crest-derived melanocytes, mast cells, osteoclasts and optic cup-derived retinal pigment epithelium. Location: Nucleus; Cytoplasm; Lysosome membrane (UniProt). Locus 3p13 (HGNC).

Where it is found
  • Skin cancer: Open Targets association 0.73 with skin cancer (MONDO_0002898)
  • Breast cancer: Open Targets association 0.59 with breast cancer (MONDO_0007254)
  • Ovarian cancer: Open Targets association 0.56 with ovarian cancer (MONDO_0008170)
  • Prostate cancer: Open Targets association 0.51 with prostate cancer (MONDO_0008315)
  • Melanoma: Open Targets association 0.75 with melanoma (MONDO_0005105); CIViC evidence names this disease
Class: transcription · Gene: MITF · Facts checked 2026-09-23 · Target page

External identifiers

Built from HGNC, Ensembl, UniProt and ChEMBL ids

Products by modality and phase

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Resistance routes

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Companion diagnostics

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Literature

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Query for this target: (TITLE:"MITF" OR ABSTRACT:"MITF" OR TITLE:"melanocyte inducing transcription factor" OR ABSTRACT:"melanocyte inducing transcription factor" OR TITLE:"Microphthalmia-associated transcription factor" OR ABSTRACT:"Microphthalmia-associated transcription factor" OR TITLE:"bHLHe32" OR ABSTRACT:"bHLHe32" OR TITLE:"WS2A" OR ABSTRACT:"WS2A" OR TITLE:"WS2" OR ABSTRACT:"WS2") AND (cancer OR tumor OR tumour OR oncology OR carcinoma OR lymphoma OR leukemia OR leukaemia OR myeloma OR sarcoma OR melanoma OR glioma). Results are unfiltered search hits about MITF, not a curated reading list.

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The dossier as machine-readable JSON: identifiers from HGNC, Ensembl, UniProt and ChEMBL, products with status, trials, pathways, hotspots, open questions and assays. The full entity record is in the open API at /api/v1/entities/mitf.json. Licence CC BY-NC 4.0.