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AZUR-1

AZUR-1 is the registrational trial of the 'no surgery, no radiation, no chemo' approach for mismatch-repair-deficient rectal cancer, built on the MSK study where every patient had a complete response.

AZUR-1 is a single-arm global trial. It met its primary objective of sustained clinical complete response at 12 months (cCR12); full data due at a 2026 congress. FDA accepted the filing with priority review and a PDUFA date of February 2027, with eligibility for the national priority voucher programme. Breakthrough designation December 2024. Follows the MSK cohort (Cercek, NEJM 2022; >40 consecutive complete responses).

Setting
Untreated stage II/III dMMR/MSI-H locally advanced rectal cancer: dostarlimab monotherapy for 6 months, no surgery or radiation if complete response
Phase
Phase 2
Sponsor
GSK
Registry
Headline result
Primary endpoint (sustained cCR at 12 months) met; rates pending congress presentation.
Reported
2026
Enrolled
154
Replication
Replicates the MSK single-centre cohort in a multicentre setting; no randomised comparison to chemoradiation and surgery exists.

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