OnCo
ideasIdea

BRAF/MEK plus PD-1 blockade as standard for BRAF-mutant anaplastic thyroid cancer

Add immunotherapy to the two targeted pills in the most aggressive thyroid cancer, because the combination has produced multi-year survivors in early series.

ATC has high PD-L1 expression and TMB; MD Anderson reports of dabrafenib-trametinib-pembrolizumab show median OS beyond 2 years in BRAF-mutant patients versus ~15 months with the doublet.

Hypothesis
Adding pembrolizumab to dabrafenib-trametinib extends OS in BRAF V600E ATC.
Rationale
Targeted therapy induces rapid immunogenic response and antigen release; ATC is immunologically hot relative to differentiated cancers.
What would test it
International randomised phase 2 (doublet vs triplet) given rarity, with OS at 12 months as primary endpoint.
Maturity
early clinical

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